Global Medical Lead LC-FAOD

Role Summary

Global Medical Lead LC-FAOD

Responsibilities

• Lead the Global Medical Sub Team (GMST), ensuring regional medical affairs are involved in and inform the development of global medical strategy
• Develop and drive the timely execution of the Global Medical Plan for LC-FAOD and triheptanoin in the pre-launch, launch, and post-launch phases
• Serve as the strategic medical leader on the Program Core Team and key sub-teams, shaping development, commercialization, and lifecycle strategies through deep scientific and clinical expertise. Work decisively to overcome challenges and drive program priorities forward
• Lead advisory boards, steering committees, and investigator meetings to gather key insights that inform program strategy and activities
• Lead updates to the Integrated Evidence Generation Plan (IEP), ensuring alignment with HEOR and clinical development to address global/regional evidence gaps
• Lead and successfully complete global medical affairs data generation activities, including real-world evidence (RWE), investigator-sponsored trials (ISTs), and other strategic evidence initiatives
• Accountable as the medical affairs lead for Disease Monitoring Programs for LC-FAOD, providing strategic medical leadership on all aspects of the study and accountable for leading data generation and publication activities aligned to the IEP
• Provide deep disease area and product expertise, ensuring accurate and consistent communication of clinical and scientific data
• Lead global publication strategy and congress planning activities, ensuring timely, high-impact dissemination of data and other education initiatives
• Lead training and provide strategic guidance and tools toregional medical affairs teams to ensure launch readiness and consistent scientific exchange
• Build and maintain relationships with global key opinion leaders, societies, and advocacy groups to inform strategy and amplify scientific reach
• Accountable for the medical assessment of the competitor environment and providing direction on strategic implications
• Collaborate effectively across the business e.g. clinical development, HEOR, diagnostics, scientific communications and publications, regulatory, market access, commercial, training, and patient advocacy

Qualifications

• Medical Doctor (MD, PhD strongly preferred) with Board Certification in Clinical/Biochemical Genetics
• Proven expertise in the management of patients with inborn errors of metabolism, preferably mitochondrial disease
• Recognized scientific authority with the ability to engage in advanced scientific and clinical discussions with both internal and external experts
• Proven leadership skills including a passion for collaboration and understanding all stakeholder perspectives to drive alignment and decision-making
• High aptitude for attention to detail, commitment to high-quality work, and a sense of passion and urgency to achieve goals and improve the lives of patients
• Proven ability to take initiative and drive successful execution of complex projects
• Highly analytical and strategic thinker with the ability to identify interdependencies, consider medical implications, and understand the broader goals of a program and the organization
• Excellent communication skills, with the ability to effectively articulate scientific and strategic concepts in both written documents and verbal presentations
• Demonstrated success leading cross functional or multidisciplinary teams, ideally in both academia and biotech
• Willingness and ability to travel up to 15%, including domestic and international engagements

Education

• Medical Doctor (MD) or PhD with Board Certification in Clinical/Biochemical Genetics