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Medical Science Liaison - Metabolism

PTC Therapeutics, Inc.
13 hours ago
On-site
Denver Metropolitan Area
Medical Affairs
Job Description Summary
The Medical Science Liaison (MSL) is a field-based Medical Affairs role that supports and represents PTC and its products with key opinion leaders (KOLs), clinicians, academic institutions, and professional organizations, by responding to unsolicited requests for information about marketed and developing products. Acts as the clinical/medical expert, builds long-term relationships, supports safe and effective product utilization, and provides input to management on market dynamics, business development, and client feedback. Works cross-functionally on Medical Affairs issues and supports adherence to relevant regulatory requirements and company SOPs.

Responsibilities
- Attend national/regional medical meetings; deliver objective clinical/scientific presentations in response to unsolicited information requests.
- Identify speakers and support advisory boards, symposia, and educational programs with regulatory-approved materials.
- Support regional medical initiatives as needed.
- Provide input on competitive therapies and business development opportunities/risks.
- Maintain relationships with health authorities (KOLs, HCPs, institutions, payors, patient organizations).
- Facilitate timely submissions for unrestricted educational grants or research initiatives per policy.
- Maintain awareness of medical/clinical, regulatory, compliance, and quality requirements.
- Maintain competitor intelligence and communicate insights to internal stakeholders.

Qualifications
- Advanced scientific degree (PhD, PharmD, MD, DNP, MSN, MS, Registered Dietician, or Genetic Counselor) plus 2+ years MSL experience or equivalent.
- Experience with orphan/rare diseases; inborn errors of metabolism/genetics/rare diseases (Phenylketonuria preferred).
- Experience with high-cost specialty pharmacy products and patient access coordination.
- Demonstrated ability to interpret scientific data and present to scientists/HCPs; strong technical/scientific writing.
- Proficiency with Microsoft Office; ability to influence without authority; analytical/problem-solving and organization skills.
- Valid driver’s license, insured personal automobile; extensive travel (50–60%), including overnight and occasional out-of-territory travel.

Preferred/Skills
- Experience supporting orphan/rare disease and/or specialized drug(s).